If approved, the new drug would be sold through the sales channels ... a gene therapy approach for HAE with Orchard Therapeutics. Leniolisib is next in line to tap into Pharming's rare disease ...

Leniolisib has been being given a speedy ... effects limiting patients' physical activity or wellbeing. If approved, the new drug would be sold through commercial channels set up by Pharming ...

CVID patients with immune dysregulation have significant clinical unmet need, with no approved therapies, and represent a significantly larger patient population. We are therefore very excited about ...