Medera Inc. (“Medera”), a clinical-stage biopharmaceutical company focused on targeting cardiovascular diseases by developing ...

Here is our list of the 11 Best Gene Therapy Stocks to Buy According to Analysts.

Marks’ resignation leaves the field without a regulator many view as “integral” to its progress over the last decade.

Three patients living with hypertrophic cardiomyopathy have had their disease classification downgraded following a single ...

Childhood-onset striatonigral degeneration is a rare genetic disorder that robs children of the ability to walk and speak by ...

Gene therapy, with its offer of a possible cure for rare diseases like sickle cell, is losing early investors to ...

Childhood-onset striatonigral neurodegeneration robs children of the ability to walk and talk by age five. Researchers at ...

A recent study led by the Universitat Autònoma de Barcelona (UAB) demonstrates the potential of gene therapy to restore motor ...

Gene therapy, a technique that is revolutionizing the treatment of multiple genetic conditions, including eye and muscle diseases and blood disorders, requires efficient and specific delivery of the ...

In a groundbreaking advancement for families grappling with the challenges of Dravet syndrome, a rare and life-altering form ...

To Novartis, fresh late-stage data support the idea that its intrathecal drug, which has the same active ingredient as ...

Shares of Sarepta Therapeutics have struggled for the past year due to concerns about the commercial potential of its gene ...